Searchable abstracts of presentations at key conferences in endocrinology

ea0063p586 | Diabetes, Obesity and Metabolism 2 | ECE2019

Real-world experience of generalized and partial lipodystrophy patients enrolled in the metreleptin early access program

Cook Keziah , Stears Anna , Araujo-Vilar David , Santini Ferruccio , O'Rahilly Stephen , Ceccarini Giovanni , Tibrewala Shruti , Bradt Pamela , Vigouroux Corinne , Vatier Camille , Savage David B

Objective: To evaluate the real-world experience of patients with generalized (GL) and partial (PL) lipodystrophy initiating treatment with metreleptin as part of an early access program (EAP).Methods: A retrospective data collection was conducted from four countries for patients enrolled in the EAP. A descriptive analysis was performed on selected patient characteristics, baseline organ impairments and complications, and response to metreleptin therapy,...